A CDMO partnership shows how gene therapy manufacturing is scaling for chronic disease
Dr. Dereck Mush, MD, MBA
Egetis Therapeutics
Rare disease drug developer behind Emcitate (tiratricol) for MCT8 deficiency.
What they do
Egetis Therapeutics develops treatments for rare diseases. On September 28, 2026 the FDA approved Emcitate (tiratricol), tablets for oral suspension, to treat peripheral thyrotoxicosis in adults and children with MCT8 deficiency (Allan-Herndon-Dudley syndrome). It is given once daily by mouth or feeding tube. The company expects US availability eight to ten weeks after approval.
The record
- Vertical
- Pharma & Drug Discovery
- Sub-segment
- Rare disease endocrinology
- Product type
- Therapeutic
- Stage
- Public
- Headquarters
- Stockholm, Sweden
- Region
- Europe
- Founded
- 2020
- Total funding
- Undisclosed
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